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Sickle β°-Thalassemia

Showing 1 - 25 of 2,120

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Pumilio1 Expression, Sickle Cell Anemia, ß-thalassemia

Not yet recruiting
  • Sickle Cell Disease, Beta Thalassemia Intermedia
  • RNA Binding Protein Pumilio1 (PUM1) Expression by reverse transcriptase quantatative PCR
  • (no location specified)
May 30, 2023

Sickle Cell Disease, Sickle Cell Trait, Beta-Thalassemia Trial (High performance liquid chromatography, Automated sickling test,

Not yet recruiting
  • Sickle Cell Disease
  • +4 more
  • High performance liquid chromatography
  • +5 more
  • (no location specified)
Aug 17, 2022

Beta-Thalassemia, Thalassemia, Hematologic Diseases Trial (CTX001)

Not yet recruiting
  • Beta-Thalassemia
  • +6 more
  • CTX001
  • (no location specified)
Jul 26, 2022

Sickle Cell Disease, Thalassemia, Beta, Thalassemia Trial in United States (Fludarabine, Cyclophosphamide, Tacrolimus)

Recruiting
  • Sickle Cell Disease
  • +2 more
  • Basking Ridge, New Jersey
  • +5 more
Feb 17, 2023

A Long-term Follow-up Study in Subjects Who Received CTX001

Enrolling by invitation
  • Beta-Thalassemia
  • +6 more
  • CTX001
  • New York, New York
  • +12 more
Nov 18, 2022

Sickle Cell Disease Trial in United Kingdom, United States (IMR-687, Placebo)

Completed
  • Sickle Cell Disease
  • Oakland, California
  • +12 more
Mar 22, 2022

Sickle Cell Disease, Beta Thalassemia-Major Trial in New Hyde Park (alemtuzumab (Campath IH), Fludarabine, Melphalan)

Completed
  • Sickle Cell Disease
  • Beta Thalassemia-Major
  • alemtuzumab (Campath IH)
  • +6 more
  • New Hyde Park, New York
    Cohen Children's Medical Center of New York
Jul 30, 2021

Sickle Cell Disease Trial in United Kingdom, United States (IMR-687)

Active, not recruiting
  • Sickle Cell Disease
  • Farmington, Connecticut
  • +6 more
Mar 2, 2022

Thalassemia Major Trial (n-acetylcystine)

Not yet recruiting
  • Thalassemia Major
  • (no location specified)
Mar 9, 2023

ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)

Recruiting
  • β-thalassemia
  • β-globin restored autologous hematopoietic stem cells
  • Shenzhen, Guangdong, China
    Shenzhen University General Hospital
May 8, 2023

Thalassemia, Beta Trial in Karachi (Hydroxyurea and Thalidomide)

Completed
  • Thalassemia, Beta
  • Hydroxyurea and Thalidomide
  • Karachi, Sindh, Pakistan
    Children's Hospital Karachi
Nov 23, 2023

ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)

Recruiting
  • β-thalassemia
  • β-globin restored autologous hematopoietic stem cells
  • Shenzhen, Guangdong, China
    Shenzhen Children's Hospital
Feb 24, 2023

ß-thalassemia Trial in Shanghai (BD211)

Not yet recruiting
  • β-thalassemia
  • BD211
  • Shanghai, China
    Shanghai Ruijin Hospital
Mar 16, 2023

Beta-Thalassemia Trial (CS-101 injection)

Not yet recruiting
  • Beta-Thalassemia
  • CS-101 injection
  • (no location specified)
Sep 27, 2023

ß-thalassemia Trial (BD211)

Not yet recruiting
  • β-thalassemia
  • BD211
  • (no location specified)
Mar 15, 2023

Beta-Thalassemia Trial in Nanning (CS-101)

Recruiting
  • Beta-Thalassemia
  • CS-101
  • Nanning, China
    The First Affiliated Hospital of Guangxi Medical University
Sep 9, 2023

Thalassemia, Beta, Thalassemia Major Trial in Tianjin (VGB-Ex01)

Not yet recruiting
  • Thalassemia, Beta
  • Thalassemia Major
  • VGB-Ex01
  • Tianjin, Tianjin, China
    Regenerative Medicine Center
Sep 11, 2023

Transfusion-dependent Beta-Thalassemia Trial in Tianjin (KL003 cell injection Drug Product)

Not yet recruiting
  • Transfusion-dependent Beta-Thalassemia
  • KL003 cell injection Drug Product
  • Tianjin, Tianjin, China
    Regenerative Medicine Center
May 8, 2023

Pulmonary Functions and Physical Fitness in ß-thalassemia

Recruiting
  • β-Thalassemia
  • +2 more
  • no intervention
  • Cairo, Egypt
    Esraa Elsayed
Aug 8, 2022

Beta Thalassemia Major Anemia Trial (SP-420)

Not yet recruiting
  • Beta Thalassemia Major Anemia
  • (no location specified)
Jan 20, 2023

Beta-thalassemia Trial in Nanning (Luspatercept, Placebo)

Recruiting
  • Beta-thalassemia
  • Nanning, China
  • +1 more
Jan 13, 2023

ß Thalassemia Major Trial in Shanghai (?-globin reactivated autologous hematopoietic stem cells)

Active, not recruiting
  • β Thalassemia Major
  • γ-globin reactivated autologous hematopoietic stem cells
  • Shanghai, Shanghai, China
    Shanghai Bioray Laboratories Inc.
Oct 9, 2022

Luspatercept in Korean Myelodysplastic Syndrome or ß-thalassemia

Not yet recruiting
  • Myelodysplastic Syndrome
  • Beta Thalassemia
  • Seoul, Korea, Republic of
    Bristol-Myers Squibb YH
Oct 3, 2023

The Prevelence of HBB c.93-21 G-A in ß Thalassemia Patients

Recruiting
  • Beta-Thalassemia
  • ARMS PCR
  • Assiut, Egypt
    Faculty of Medicine Assiut University
Jan 30, 2023

Sickle Cell Anemia, Beta Thalassemia Trial run by the NHLBI (radiation, drug, biological)

Recruiting
  • Sickle Cell Anemia
  • Beta Thalassemia
  • TBI
  • +6 more
  • Bethesda, Maryland
    National Institutes of Health Clinical Center
Jan 26, 2023