Sickle β°-Thalassemia
Showing 1 - 25 of 2,120
Pumilio1 Expression, Sickle Cell Anemia, ß-thalassemia
Not yet recruiting
- Sickle Cell Disease, Beta Thalassemia Intermedia
- RNA Binding Protein Pumilio1 (PUM1) Expression by reverse transcriptase quantatative PCR
- (no location specified)
May 30, 2023
Sickle Cell Disease, Sickle Cell Trait, Beta-Thalassemia Trial (High performance liquid chromatography, Automated sickling test,
Not yet recruiting
- Sickle Cell Disease
- +4 more
- High performance liquid chromatography
- +5 more
- (no location specified)
Aug 17, 2022
Beta-Thalassemia, Thalassemia, Hematologic Diseases Trial (CTX001)
Not yet recruiting
- Beta-Thalassemia
- +6 more
- CTX001
- (no location specified)
Jul 26, 2022
Sickle Cell Disease, Thalassemia, Beta, Thalassemia Trial in United States (Fludarabine, Cyclophosphamide, Tacrolimus)
Recruiting
- Sickle Cell Disease
- +2 more
- Fludarabine
- +7 more
-
Basking Ridge, New Jersey
- +5 more
Feb 17, 2023
A Long-term Follow-up Study in Subjects Who Received CTX001
Enrolling by invitation
- Beta-Thalassemia
- +6 more
- CTX001
-
New York, New York
- +12 more
Nov 18, 2022
Sickle Cell Disease, Beta Thalassemia-Major Trial in New Hyde Park (alemtuzumab (Campath IH), Fludarabine, Melphalan)
Completed
- Sickle Cell Disease
- Beta Thalassemia-Major
- alemtuzumab (Campath IH)
- +6 more
-
New Hyde Park, New YorkCohen Children's Medical Center of New York
Jul 30, 2021
ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)
Recruiting
- β-thalassemia
- β-globin restored autologous hematopoietic stem cells
-
Shenzhen, Guangdong, ChinaShenzhen University General Hospital
May 8, 2023
Thalassemia, Beta Trial in Karachi (Hydroxyurea and Thalidomide)
Completed
- Thalassemia, Beta
- Hydroxyurea and Thalidomide
-
Karachi, Sindh, PakistanChildren's Hospital Karachi
Nov 23, 2023
ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)
Recruiting
- β-thalassemia
- β-globin restored autologous hematopoietic stem cells
-
Shenzhen, Guangdong, ChinaShenzhen Children's Hospital
Feb 24, 2023
ß-thalassemia Trial in Shanghai (BD211)
Not yet recruiting
- β-thalassemia
- BD211
-
Shanghai, ChinaShanghai Ruijin Hospital
Mar 16, 2023
Beta-Thalassemia Trial (CS-101 injection)
Not yet recruiting
- Beta-Thalassemia
- CS-101 injection
- (no location specified)
Sep 27, 2023
ß-thalassemia Trial (BD211)
Not yet recruiting
- β-thalassemia
- BD211
- (no location specified)
Mar 15, 2023
Beta-Thalassemia Trial in Nanning (CS-101)
Recruiting
- Beta-Thalassemia
- CS-101
-
Nanning, ChinaThe First Affiliated Hospital of Guangxi Medical University
Sep 9, 2023
Thalassemia, Beta, Thalassemia Major Trial in Tianjin (VGB-Ex01)
Not yet recruiting
- Thalassemia, Beta
- Thalassemia Major
- VGB-Ex01
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
Sep 11, 2023
Transfusion-dependent Beta-Thalassemia Trial in Tianjin (KL003 cell injection Drug Product)
Not yet recruiting
- Transfusion-dependent Beta-Thalassemia
- KL003 cell injection Drug Product
-
Tianjin, Tianjin, ChinaRegenerative Medicine Center
May 8, 2023
Pulmonary Functions and Physical Fitness in ß-thalassemia
Recruiting
- β-Thalassemia
- +2 more
- no intervention
-
Cairo, EgyptEsraa Elsayed
Aug 8, 2022
ß Thalassemia Major Trial in Shanghai (?-globin reactivated autologous hematopoietic stem cells)
Active, not recruiting
- β Thalassemia Major
- γ-globin reactivated autologous hematopoietic stem cells
-
Shanghai, Shanghai, ChinaShanghai Bioray Laboratories Inc.
Oct 9, 2022
Luspatercept in Korean Myelodysplastic Syndrome or ß-thalassemia
Not yet recruiting
- Myelodysplastic Syndrome
- Beta Thalassemia
-
Seoul, Korea, Republic ofBristol-Myers Squibb YH
Oct 3, 2023
The Prevelence of HBB c.93-21 G-A in ß Thalassemia Patients
Recruiting
- Beta-Thalassemia
- ARMS PCR
-
Assiut, EgyptFaculty of Medicine Assiut University
Jan 30, 2023
Sickle Cell Anemia, Beta Thalassemia Trial run by the NHLBI (radiation, drug, biological)
Recruiting
- Sickle Cell Anemia
- Beta Thalassemia
- TBI
- +6 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 26, 2023